Meet the family seeking to fund research into a rare disease that afflicts their two boys. In this webinar, Ed Boyden and Jerzy Szablowski will talk about how synthetic biology can help develop tools ...

Twenty years ago, Ilyce Randell and her husband received devastating news: their son Maxie, who was a little over four months old at the time, had Canavan disease. Maxie would never walk or talk ...

and Canavan disease, both of which result from mutations in enzymes in the sulphatide pathway. There are no cures for these diseases, which are typically treated with enzyme-replacement therapy ...

WE WERE QUITE LITERALLY THE FIRST PEOPLE TO BE TOLD LIKE, HERE’S SOMETHING THAT YOU CAN HAVE SOME, SOME, SOME HOPE. DOCTORS AT UMASS CHAN MEDICAL SCHOOL BEGAN WORKING ON CANAVAN DISEASE IN 1989.