Featured data showcase the transformative potential of HSC gene therapy to enable cross-correction and restore enzymatic ...

The first baby to have a cord blood sample taken as part of the study at Jessop Wing was Sophia Bird, who was born on ...

Orchard Therapeutics has revealed its US pricing plans for Lenmeldy, its gene therapy for metachromatic leukodystrophy (MLD), placing a $4.25 million price tag on the one-shot treatment.

Among these innovations, if there is one name that is gaining a lot of attention recently in the medical field, it is ...

Vice-chancellor of London's prestigious King's College, Prof. Shitij Kapur busts myths around longevity hacks and advocates ...

Libmeldy (atidarsagene autotemcel) was approved by the European Commission to treat metachromatic leukodystrophy (MLD) in December 2020, and subsequently rejected for NHS use by NICE last July on ...

By Cailin RileyCommunicating how he feels has never been easy for Hunter Gladding. The 7-year-old East Quogue resident was ...

After hours: February 3 at 5:20:37 PM EST Loading Chart for PASG ...

The review was based on a PubMed search (search terms: ‘spinal cord’ AND ‘leukoencephalopathy’ OR ‘leukodystrophy’; ‘spinal cord’ AND ‘vitamin ... roots and cauda equina could be found in ...