A funny thing people do when you tell them a sad story is offer a consolation prize. There’s a special one for mothers mired in misfortune: You win the honor of being called “strong.” Even though you ...
From Adrenoleukodystrophy to Zollinger Ellison Syndrome, there are currently over 7,000 diseases identified as rare. In the U.S., the Orphan Drug Act of 1983 defines a disease as “rare” if it affects ...
It is either tragically funny or devastatingly sad that while a genetic counselor explained the random lunacy of my son’s deadly disease to me all I could think of was how our current situation bears ...
VK-2735 is under clinical development by Viking Therapeutics and currently in Phase II for Obesity. According to GlobalData, Phase II drugs for Obesity have a 29% phase transition success rate (PTSR) ...
So it was especially painful when we found out shortly after he was born nine months ago that my youngest, William, has a rare genetic disorder called Adrenoleukodystrophy, or ALD.
It’s a rare genetic disorder that impacts a small population, and due to limited research, much remains unknown about treating adrenoleukodystrophy. Now, there’s a new multi-million-dollar fund ...
and offering hope to families affected by X-Linked Adrenoleukodystrophy (ALD), all in pursuit of a cure for their loved ones. ALD is a genetic condition, impacting 1-in-17,000 births, that affects ...